Preclinical development and qualification of ZFN-mediated CCR5 disruption in human hematopoietic stem/progenitor cells

DiGiusto D, Canno P, Holmes M, Li L, et al. Preclinical development and qualification of ZFN-mediated CCR5 disruption in human hematopoietic stem/progenitor cells. Molecular Therapy — Methods & Clinical Development 3, Article number: 16067 (2016) doi:10.1038/mtm.2016.67

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